Until now there has been no treatment. But on Wednesday researchers reported how a new gene therapy had managed to slow progress of the disease by 75%.

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[–] 26 points 1 year ago (6 children)

Very good news! I hope the treatment will be relatively inexpensive for all.

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  • [–] 16 points 1 year ago (4 children)

    Well, it will not. It will cost >US$3M, and few countries could even handle the number of surgeries required.

    Shame on the BBC and their unbridled hype on this. You will need to win the lottery ten times over to pay for this.

    But this is a SINGLE UNCONTROLLED trial and not approved. Once again, HD families are being hyped on a therapy will little public release of data. This is not the first time a "cure" goes practically nowhere for this disease. And again, the same two British researchers in front of this hyping as they did in the past. This is extremely unprofessional and irresponsible.

    People got very rich off QURE stock this week.

    The concept is promising. There was a much cheaper oral drug that showed similar efficacy in phase two trials this summer and the media ignored it. Lazy journalism or a clear agenda, not sure what is going on. There is a real drug further along the approval pipeline that will not be just for billionaires. Somehow the BBC doesn't know this.

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  • [–] 5 points 1 year ago (1 child)

    There was a much cheaper oral drug that showed similar efficacy in phase two trials this summer and the media ignored it.

    Which drug is that? You’re not kidding about “media ignored it” I tried searching and found nothing.

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  • [–] 13 points 1 year ago

    That's fucking incredible

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  • [+] 13 points 1 year ago (1 child)
  • [–] 10 points 1 year ago

    Heard this news on a podcast a few days ago, and I had to actually stop making breakfast and listen to it because it was just so amazing. This is incredible news!

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  • You'd have to win the lottery to afford it, especially in the United States.

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  • [–] 6 points 1 year ago

    What an incredible discovery. Quite nice to see news like this with all that crap that's going on in the world.

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